Technique makes gene therapy permanent

This sounds exciting: Mount Sinai School of Medicine researchers have developed a technique for inserting genes into specific non-coding regions of the genome in liver cells. Because these regions occur between genes, there’s no danger of the insertion damanging existing genes–and the inserted gene becomes a permanent part of the genome.

Using this technique, the researchers cured a condition called phenylketonuria (PKU) in mice.

Could this be the breakthrough that makes the enormous promise of gene therapy a reality?

Permanent link to this article: https://edwardwillett.com/2005/10/technique-makes-gene-therapy-permanent/

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